Meeting report of the 226th ENMC workshop towards validated and qualified biomarkers for therapy development for duchenne muscular dystrophy 20-22 january 2017, heemskerk, the netherlands


• Biomarker validation and qualification requires collaboration of all stakeholders• Consensus was reached on criteria candidate biomarkers need to fulfil• Alignment was reached on a proposed path for regulatory qualification for MRI• A virtual biobank is needed for biomarker discovery and validation


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