Functional variability among boys with Duchenne muscular dystrophy (DMD) is well recognized and complicates the interpretation of clinical studies. To further understanding, we assessed whether boys with DMD could be clustered into groups sharing similar trajectories of ambulatory function over time, as measured by the North Star Ambulatory Assessment (NSAA) total score, and then explored associations with other factors. Using the North Star Clinical Network database (23 UK centres) we identified 337 genotyped patients with >1 NSAA assessment.

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