Duchenne muscular dystrophy (DMD) is an X-linked recessive disorder occurring in 1 in 4000 live male births [1]. DMD is a life-limiting disorder associated with progressive muscle inflammation, degeneration, fatty infiltration and fibrosis leading to progressive motor disability. Most affected boys will be wheel chair dependent by the age of 12 years. Glucocorticoid (GC) therapy is the only disease-modifying option, which has been shown to improve short-term muscle function and strength [2] but other benefits including preservation of upper limb function, reduction in risk of scoliosis and preservation of cardiac function are reported with prolonged use [3–5].

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